Atlanta, GA5 Active Studies

Fabry Disease Clinical Trials in Atlanta, GA

Find 5 actively recruiting fabry disease clinical trials in Atlanta, GA. Connect with local research sites and explore new treatment options.

5
Active Trials
3
Sponsors
592
Enrolling

Recruiting Fabry Disease Studies in Atlanta

NCT06906367Recruiting

A Study of Patients With Fabry Disease (US Specific)

This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on ...

Atlanta, GA450 participantsAmicus Therapeutics
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NCT06663358Recruiting

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

A multi-centre, multi-country, observational, non-interventional, retrospective and prospective (hybrid) study among Fabry disease participants treated with pegunigalsidase alfa (Elfabrio®) in routine...

Atlanta, GA100 participantsChiesi Farmaceutici S.p.A.
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NCT06328608Recruiting

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents with Fabry Disease....

Atlanta, GAPHASE222 participantsChiesi Farmaceutici S.p.A.
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NCT06270316Recruiting

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

The main goals of this clinical study are to characterize safety and PK/PD of AMT-191 i.e. if drug doses used in the study are safe and tolerable and to understand how it acts in the body of people wi...

Atlanta, GAPHASE112 participantsUniQure Biopharma B.V.
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NCT06904261Recruiting

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

An open-label study to evaluate the safety, pharmacokinetics (PK), pharmacodynamics (PD), and efficacy of migalastat treatment in pediatric subjects 2 to \< 12 years of age with Fabry disease and with...

Atlanta, GAPHASE38 participantsAmicus Therapeutics
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About Fabry Disease Clinical Trials in Atlanta

Fabry disease is a rare genetic disorder caused by deficiency of the enzyme alpha-galactosidase A, leading to accumulation of a fatty substance in cells. It can affect the heart, kidneys, and nervous system. Treatment includes enzyme replacement therapy and chaperone therapy.

There are currently 5 fabry disease clinical trials recruiting participants in Atlanta, GA. These studies are seeking a combined 592 participants. Research is being sponsored by Amicus Therapeutics, Chiesi Farmaceutici S.p.A., UniQure Biopharma B.V.. Clinical trial participation is free and participants receive study-related medical care at no cost.

Fabry Disease Clinical Trials in Atlanta — FAQ

Are there fabry disease clinical trials in Atlanta?

Yes, there are 5 fabry disease clinical trials currently recruiting in Atlanta, GA. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Atlanta?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Atlanta research site will contact you about next steps.

Are clinical trials in Atlanta free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Atlanta studies also compensate for your time and travel.

What fabry disease treatments are being tested?

The 5 active trials in Atlanta are testing new therapies including novel drugs, biologics, and treatment approaches for fabry disease.

Data updated August 28, 2026 from ClinicalTrials.gov