Recruiting Batten Disease Studies in Bethesda
About Batten Disease Clinical Trials in Bethesda
Batten disease refers to a group of rare, inherited neurological disorders (neuronal ceroid lipofuscinoses) that cause progressive loss of vision, cognition, and motor skills. They primarily affect children. Gene therapy and enzyme replacement therapy are being studied as potential treatments.
There are currently 1 batten disease clinical trials recruiting participants in Bethesda, MD. These studies are seeking a combined 300 participants. Research is being sponsored by Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD). Clinical trial participation is free and participants receive study-related medical care at no cost.
Batten Disease Clinical Trials in Bethesda — FAQ
Are there batten disease clinical trials in Bethesda?
Yes, there are 1 batten disease clinical trials currently recruiting in Bethesda, MD. Browse the studies on this page to find one that fits.
How do I join a clinical trial in Bethesda?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Bethesda research site will contact you about next steps.
Are clinical trials in Bethesda free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Bethesda studies also compensate for your time and travel.
What batten disease treatments are being tested?
The 1 active trials in Bethesda are testing new therapies including novel drugs, biologics, and treatment approaches for batten disease.
Data updated October 16, 2026 from ClinicalTrials.gov