6 Duchenne Muscular Dystrophy Clinical Trials in Gainesville, FL (2026)

Q: How do I join a clinical trial in Gainesville?

Browse available studies, click one that interests you, and complete the free eligibility form. A study coordinator at the Gainesville research site will contact you.

Recruiting Duchenne Muscular Dystrophy Studies in Gainesville

NCT01484678Recruiting

Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy

The purpose of this research study is to determine the potential of magnetic resonance imaging, spectroscopy, and whole body imaging to monitor disease progression and to serve as an objective outcome...

Gainesville, FL550 participantsUniversity of Florida

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NCT06564974Recruiting

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

The goal of this study is to collect additional information on the safety of long-term treatment with AGAMREE® and to explore long-term clinical impact of AGAMREE® on quality of life, as assessed by s...

Gainesville, FL250 participantsCatalyst Pharmaceuticals, Inc.

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NCT03373968Recruiting

Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study

This is an open label, long-term safety, tolerability, and efficacy study of GIVINOSTAT in all DMD (Duchenne's muscular dystrophy) patients who have been previously treated in one of the GIVINOSTAT st...

Gainesville, FL206 participantsItalfarmaco

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NCT07038200Recruiting

A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD

A Randomized, Double-blind, Placebo-controlled, Phase 3 Study to Evaluate the Efficacy and Safety of Intravenous AOC 1020 for the Treatment of Facioscapulohumeral Muscular Dystrophy (FSHD)...

Gainesville, FL200 participantsAvidity Biosciences, Inc.

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NCT05693142Recruiting

AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)

RGX-202 is a gene therapy designed to deliver a transgene for a novel microdystrophin that includes functional elements of naturally-occurring dystrophin including the C-Terminal (CT) domain. This is...

Gainesville, FL65 participantsREGENXBIO Inc.

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NCT06290713Recruiting

Vasodilator and Exercise Study for DMD (VASO-REx)

Examining two strategies as potential adjuvant therapies for Duchenne muscular dystrophy (DMD); aerobic exercise training (to induce adaptations in skeletal muscle and improve cardiovascular health) a...

Gainesville, FL50 participantsUniversity of Florida

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About Duchenne Muscular Dystrophy Clinical Trials in Gainesville

Duchenne muscular dystrophy is a severe genetic disorder characterized by progressive muscle degeneration and weakness, primarily affecting boys. It is caused by mutations in the dystrophin gene. Treatment includes corticosteroids, gene therapies, and supportive care to maintain mobility and function.

There are currently 6 duchenne muscular dystrophy clinical trials recruiting participants in Gainesville, FL. These studies are seeking a combined 1,321 participants. Research is being sponsored by University of Florida, Catalyst Pharmaceuticals, Inc., Italfarmaco and 2 other organizations. Clinical trial participation is free and participants receive study-related medical care at no cost.

Duchenne Muscular Dystrophy Clinical Trials in Gainesville — FAQ

Are there duchenne muscular dystrophy clinical trials in Gainesville?

Yes, there are 6 duchenne muscular dystrophy clinical trials currently recruiting in Gainesville, FL. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Gainesville?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Gainesville research site will contact you about next steps.

Are clinical trials in Gainesville free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Gainesville studies also compensate for your time and travel.

What duchenne muscular dystrophy treatments are being tested?

The 6 active trials in Gainesville are testing new therapies including novel drugs, biologics, and treatment approaches for duchenne muscular dystrophy.

Data updated July 13, 2026 from ClinicalTrials.gov