Recruiting Rett Syndrome Studies in La Jolla
To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
Primary Objective • To investigate the efficacy of treatment with oral Bionetide versus placebo in girls and women with Rett syndrome Key Secondary Objective • To investigate the efficacy of treatme...
Safety and Efficacy of TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study)
The REVEAL Pediatric Study is a multi-center, Phase 1/2 open-label, dose-escalation and dose-expansion study of TSHA-102, an investigational gene therapy, in pediatric females with Rett Syndrome. The...
Safety and Efficacy of TSHA-102 in Adolescent and Adult Females With Rett Syndrome (REVEAL Adult Study)
The REVEAL Adult Study is a multi-center, Phase 1/2 open-label, dose-escalation study of TSHA-102, an investigational gene therapy, in adult females with Rett syndrome. The safety, tolerability, and p...
About Rett Syndrome Clinical Trials in La Jolla
Rett syndrome is a rare genetic neurological disorder that primarily affects girls, causing a regression in development after initially normal growth. It is caused by mutations in the MECP2 gene. Treatment is supportive, with gene therapies under investigation.
There are currently 3 rett syndrome clinical trials recruiting participants in La Jolla, CALIFORNIA. These studies are seeking a combined 248 participants. Research is being sponsored by Biomed Industries, Inc., Taysha Gene Therapies, Inc.. Clinical trial participation is free and participants receive study-related medical care at no cost.
Rett Syndrome Clinical Trials in La Jolla — FAQ
Are there rett syndrome clinical trials in La Jolla?
Yes, there are 3 rett syndrome clinical trials currently recruiting in La Jolla, CALIFORNIA. Browse the studies on this page to find one that fits.
How do I join a clinical trial in La Jolla?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the La Jolla research site will contact you about next steps.
Are clinical trials in La Jolla free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many La Jolla studies also compensate for your time and travel.
What rett syndrome treatments are being tested?
The 3 active trials in La Jolla are testing new therapies including novel drugs, biologics, and treatment approaches for rett syndrome.
Data updated March 2, 2026 from ClinicalTrials.gov