11 Duchenne Muscular Dystrophy Clinical Trials in Little Rock, AR (2026)

Q: How do I join a clinical trial in Little Rock?

Browse available studies, click one that interests you, and complete the free eligibility form. A study coordinator at the Little Rock research site will contact you.

Recruiting Duchenne Muscular Dystrophy Studies in Little Rock

NCT04972604Recruiting

CureDuchenne Link®: A Resource for Research

CureDuchenne link is a data hub comprised of integrated biospecimens, clinical data, and self- and/or caregiver-reported information from participants. Anyone over 4 weeks old who has been diagnosed w...

Little Rock, AR5,000 participantsCureDuchenne

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NCT07609394Recruiting

Duchenne Electronic Health Record Study

This study aims to collect retrospective and prospective, long-term data of patients with dystrophinopathy (including Duchenne, Becker, and female carriers) through electronic transfer. At select clin...

Little Rock, AR2,500 participantsThe Duchenne Registry

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NCT07127978Recruiting

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

This is a prospective observational study conducted to evaluate safety, tolerability, and functional outcomes of patients with DMD newly initiating oral givinostat or having started therapy within 6 m...

Little Rock, AR300 participantsITF Therapeutics LLC

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NCT06564974Recruiting

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

The goal of this study is to collect additional information on the safety of long-term treatment with AGAMREE® and to explore long-term clinical impact of AGAMREE® on quality of life, as assessed by s...

Little Rock, AR250 participantsCatalyst Pharmaceuticals, Inc.

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NCT04626674Recruiting

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

Cohort 8 (non-ambulatory participants) is currently enrolling new participants. Enrollment for Cohorts 1 through 7 has been completed. This is an open-label gene transfer therapy study evaluating the...

Little Rock, AR83 participantsSarepta Therapeutics, Inc.

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NCT07160634Recruiting

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

This is a Phase 3, double-blind, placebo-controlled study with the primary objective of evaluating the efficacy of a single IV infusion of SGT-003 in pediatric ambulant male participants with DMD. The...

Little Rock, AR80 participantsSolid Biosciences Inc.

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NCT05693142Recruiting

AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)

RGX-202 is a gene therapy designed to deliver a transgene for a novel microdystrophin that includes functional elements of naturally-occurring dystrophin including the C-Terminal (CT) domain. This is...

Little Rock, AR65 participantsREGENXBIO Inc.

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NCT06138639Recruiting

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

This is a multicenter, open-label, non-randomized study to investigate the safety, tolerability, and efficacy of a single intravenous (IV) infusion of SGT-003 in participants with Duchenne muscular dy...

Little Rock, AR60 participantsSolid Biosciences Inc.

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NCT04906460Recruiting

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

This is a Phase 1b/2 open-label study to evaluate the safety, tolerability, pharmacokinetic (PK), pharmacodynamic (PD), and clinical effects of intravenous (IV) WVE-N531 in patients with Duchenne musc...

Little Rock, AR26 participantsWave Life Sciences USA, Inc.

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NCT07429240Recruiting

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

The purpose of this Phase 1/2a trial is to evaluate the safety, tolerability, and preliminary efficacy of PBGENE-DMD in patients with DMD harboring mutations amenable to excision of exons 45-55. Given...

Little Rock, AR18 participantsPrecision BioSciences, Inc.

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NCT06817382Recruiting

A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

The primary objective of this study is to evaluate the safety and tolerability of a single dose of INS1201 via IT administration in ambulatory male participants with DMD....

Little Rock, AR12 participantsInsmed Gene Therapy LLC

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About Duchenne Muscular Dystrophy Clinical Trials in Little Rock

Duchenne muscular dystrophy is a severe genetic disorder characterized by progressive muscle degeneration and weakness, primarily affecting boys. It is caused by mutations in the dystrophin gene. Treatment includes corticosteroids, gene therapies, and supportive care to maintain mobility and function.

There are currently 11 duchenne muscular dystrophy clinical trials recruiting participants in Little Rock, AR. These studies are seeking a combined 8,394 participants. Research is being sponsored by CureDuchenne, The Duchenne Registry, ITF Therapeutics LLC and 7 other organizations. Clinical trial participation is free and participants receive study-related medical care at no cost.

Duchenne Muscular Dystrophy Clinical Trials in Little Rock — FAQ

Are there duchenne muscular dystrophy clinical trials in Little Rock?

Yes, there are 11 duchenne muscular dystrophy clinical trials currently recruiting in Little Rock, AR. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Little Rock?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Little Rock research site will contact you about next steps.

Are clinical trials in Little Rock free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Little Rock studies also compensate for your time and travel.

What duchenne muscular dystrophy treatments are being tested?

The 11 active trials in Little Rock are testing new therapies including novel drugs, biologics, and treatment approaches for duchenne muscular dystrophy.

Data updated July 13, 2026 from ClinicalTrials.gov