Recruiting Batten Disease Studies in Pittsburgh
About Batten Disease Clinical Trials in Pittsburgh
Batten disease refers to a group of rare, inherited neurological disorders (neuronal ceroid lipofuscinoses) that cause progressive loss of vision, cognition, and motor skills. They primarily affect children. Gene therapy and enzyme replacement therapy are being studied as potential treatments.
There are currently 1 batten disease clinical trials recruiting participants in Pittsburgh, PA. These studies are seeking a combined 60 participants. Research is being sponsored by Jorge Gonzalez-Martinez. Clinical trial participation is free and participants receive study-related medical care at no cost.
Batten Disease Clinical Trials in Pittsburgh — FAQ
Are there batten disease clinical trials in Pittsburgh?
Yes, there are 1 batten disease clinical trials currently recruiting in Pittsburgh, PA. Browse the studies on this page to find one that fits.
How do I join a clinical trial in Pittsburgh?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Pittsburgh research site will contact you about next steps.
Are clinical trials in Pittsburgh free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Pittsburgh studies also compensate for your time and travel.
What batten disease treatments are being tested?
The 1 active trials in Pittsburgh are testing new therapies including novel drugs, biologics, and treatment approaches for batten disease.
Data updated October 16, 2026 from ClinicalTrials.gov