Recruiting Angelman Syndrome Studies in Randwick
About Angelman Syndrome Clinical Trials in Randwick
Angelman syndrome is a rare genetic disorder primarily affecting the nervous system, characterized by severe developmental delays, speech impairment, seizures, and a happy demeanor. It is caused by loss of function of the UBE3A gene. Treatment focuses on managing symptoms and maximizing developmental potential.
There are currently 1 angelman syndrome clinical trials recruiting participants in Randwick, NEW%20SOUTH%20WALES. These studies are seeking a combined 70 participants. Research is being sponsored by Ionis Pharmaceuticals, Inc.. Clinical trial participation is free and participants receive study-related medical care at no cost.
Angelman Syndrome Clinical Trials in Randwick — FAQ
Are there angelman syndrome clinical trials in Randwick?
Yes, there are 1 angelman syndrome clinical trials currently recruiting in Randwick, NEW%20SOUTH%20WALES. Browse the studies on this page to find one that fits.
How do I join a clinical trial in Randwick?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Randwick research site will contact you about next steps.
Are clinical trials in Randwick free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Randwick studies also compensate for your time and travel.
What angelman syndrome treatments are being tested?
The 1 active trials in Randwick are testing new therapies including novel drugs, biologics, and treatment approaches for angelman syndrome.
Data updated March 2, 2026 from ClinicalTrials.gov