Recruiting Batten Disease Studies in Rochester
About Batten Disease Clinical Trials in Rochester
Batten disease refers to a group of rare, inherited neurological disorders (neuronal ceroid lipofuscinoses) that cause progressive loss of vision, cognition, and motor skills. They primarily affect children. Gene therapy and enzyme replacement therapy are being studied as potential treatments.
There are currently 1 batten disease clinical trials recruiting participants in Rochester, NY. These studies are seeking a combined 500 participants. Research is being sponsored by University of Rochester. Clinical trial participation is free and participants receive study-related medical care at no cost.
Batten Disease Clinical Trials in Rochester — FAQ
Are there batten disease clinical trials in Rochester?
Yes, there are 1 batten disease clinical trials currently recruiting in Rochester, NY. Browse the studies on this page to find one that fits.
How do I join a clinical trial in Rochester?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Rochester research site will contact you about next steps.
Are clinical trials in Rochester free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Rochester studies also compensate for your time and travel.
What batten disease treatments are being tested?
The 1 active trials in Rochester are testing new therapies including novel drugs, biologics, and treatment approaches for batten disease.
Data updated October 16, 2026 from ClinicalTrials.gov