Recruiting Pompe Disease Studies in Salt Lake City
A Study of mRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a)
The main goal of this trial is to evaluate the safety and tolerability of mRNA-3745 via intravenous (IV) administration in adult and pediatric participants with GSD1a....
A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
This is a Phase 3, open-label, multicenter study to evaluate the safety, efficacy, PK, PD, and immunogenicity of cipaglucosidase alfa/miglustat treatment in ERT-experienced and ERT-naïve pediatric sub...
About Pompe Disease Clinical Trials in Salt Lake City
Pompe disease is a rare genetic disorder caused by accumulation of glycogen in cells due to deficiency of the enzyme acid alpha-glucosidase. It can affect the heart, skeletal muscles, and respiratory system. Treatment includes enzyme replacement therapy.
There are currently 2 pompe disease clinical trials recruiting participants in Salt Lake City, UTAH. These studies are seeking a combined 81 participants. Research is being sponsored by ModernaTX, Inc., Amicus Therapeutics. Clinical trial participation is free and participants receive study-related medical care at no cost.
Pompe Disease Clinical Trials in Salt Lake City — FAQ
Are there pompe disease clinical trials in Salt Lake City?
Yes, there are 2 pompe disease clinical trials currently recruiting in Salt Lake City, UTAH. Browse the studies on this page to find one that fits.
How do I join a clinical trial in Salt Lake City?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Salt Lake City research site will contact you about next steps.
Are clinical trials in Salt Lake City free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Salt Lake City studies also compensate for your time and travel.
What pompe disease treatments are being tested?
The 2 active trials in Salt Lake City are testing new therapies including novel drugs, biologics, and treatment approaches for pompe disease.
Data updated March 2, 2026 from ClinicalTrials.gov