Recruiting Pompe Disease Studies in St Louis
About Pompe Disease Clinical Trials in St Louis
Pompe disease is a rare genetic disorder caused by accumulation of glycogen in cells due to deficiency of the enzyme acid alpha-glucosidase. It can affect the heart, skeletal muscles, and respiratory system. Treatment includes enzyme replacement therapy.
There are currently 1 pompe disease clinical trials recruiting participants in St Louis, MO. These studies are seeking a combined 22 participants. Research is being sponsored by Amicus Therapeutics. Clinical trial participation is free and participants receive study-related medical care at no cost.
Pompe Disease Clinical Trials in St Louis — FAQ
Are there pompe disease clinical trials in St Louis?
Yes, there are 1 pompe disease clinical trials currently recruiting in St Louis, MO. Browse the studies on this page to find one that fits.
How do I join a clinical trial in St Louis?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the St Louis research site will contact you about next steps.
Are clinical trials in St Louis free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many St Louis studies also compensate for your time and travel.
What pompe disease treatments are being tested?
The 1 active trials in St Louis are testing new therapies including novel drugs, biologics, and treatment approaches for pompe disease.
Data updated March 2, 2026 from ClinicalTrials.gov