Access cutting-edge pompe disease treatment through this clinical trial at a research site in Fairfax. Study-provided care at no cost to qualified participants.
Access pompe disease specialists in Fairfax at no cost
This study follows strict safety protocols and ethical guidelines
All study-related pompe disease treatment provided free
This is a Phase 3, open-label, multicenter study to evaluate the safety, PK, efficacy, PD, and immunogenicity of Cipaglucosidase Alfa/Miglustat treatment in enzyme replacement therapy (ERT)-experienced and ERT-naïve pediatric subjects with Pompe disease, aged 0 to \< 18 years
Sponsor: Amicus Therapeutics
Check if you qualify for this pompe disease clinical trial in Fairfax, VA
If you're searching for pompe disease treatment options in Fairfax, VA, this clinical trial may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.
Our Fairfax research site is actively enrolling participants for this clinical trial. You'll receive care from experienced pompe disease specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.