Access cutting-edge glycogen storage disease treatment through this clinical trial at a research site in Orange. Study-provided care at no cost to qualified participants.
Access glycogen storage disease specialists in Orange at no cost
This study follows strict safety protocols and ethical guidelines
All study-related glycogen storage disease treatment provided free
This is a Phase 1/2, multicenter, open-label, single-ascending-dose study to evaluate the safety, tolerability, and efficacy of BEAM-301 in adult patients with GSDIa homozygous or compound heterozygous for the G6PC1 c.247C\>T (p.R83C) variant and to determine the optimal biological dose.
Sponsor: Beam Therapeutics Inc.
Check if you qualify for this glycogen storage disease clinical trial in Orange, CA
If you're searching for glycogen storage disease treatment options in Orange, CA, this clinical trial may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.
Our Orange research site is actively enrolling participants for this clinical trial. You'll receive care from experienced glycogen storage disease specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.