Rancho Santa Margarita, CANCT04917887Now EnrollingIRB Ready

Dystrophic Epidermolysis Bullosa Clinical Trial in Rancho Santa Margarita, CA

Access cutting-edge dystrophic epidermolysis bullosa treatment through this clinical trial at a research site in Rancho Santa Margarita. Study-provided care at no cost to qualified participants.

Sponsored by Krystal Biotech, Inc.

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Expert Care in Rancho Santa Margarita

Access dystrophic epidermolysis bullosa specialists at no cost

IRB Approved

This study follows strict safety protocols and ethical guidelines

No-Cost Care

All study-related dystrophic epidermolysis bullosa treatment provided free

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Check if you qualify for this dystrophic epidermolysis bullosa clinical trial in Rancho Santa Margarita, CA

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Why Participate?

  • No-Cost Study Care

  • Local to Rancho Santa Margarita

    Convenient for CA residents

  • Cutting-Edge Treatment

    Access to innovative therapies

  • Expert Medical Care

    Close monitoring by specialists

  • Possible Compensation*

    For time and travel

*Compensation varies by study. Confirm details with coordinator.

Simple Process

  1. 1Submit this form
  2. 2Phone screening
  3. 3Visit Rancho Santa Margarita site if eligible
  4. 4Begin participation

About This Dystrophic Epidermolysis Bullosa Study in Rancho Santa Margarita

The main objective of this prospective, observational, long-term follow-up (LTFU) study is to evaluate the long-term safety profile of the gene therapy products evaluated by Krystal Biotech, Inc. which have a shared backbone of HSV-1, in participants who received at least one dose of investigational product (IP).

Sponsor: Krystal Biotech, Inc.

Who Can Participate

Inclusion Criteria

All adult and pediatric participants who received at least one gene therapy treatment in a previous Krystal Biotech, Inc. sponsored study, and have discontinued or completed the parent treatment protocol (which do not have the LTFU embedded into the parent protocol), as applicable.
Consent/Assent must be obtained by the participants (and, parental/legal representative, when applicable) prior to any study-related data being collected.
Participant is willing and able to adhere to the protocol requirements.

Exclusion Criteria

Participants who enroll into a non-Krystal Biotech, Inc. interventional gene therapy clinical trial will be excluded from the study.

Not sure if you qualify? Submit your interest and a study coordinator will help determine your eligibility.

Frequently Asked Questions

Q:Is this study available in Rancho Santa Margarita?

Yes, this clinical trial (NCT04917887) has an active research site in Rancho Santa Margarita, CA that is currently enrolling participants.

Q:Is it safe to participate?

Clinical trials follow strict safety guidelines and ethical standards. This study has been reviewed and approved, and participants are closely monitored by medical professionals. You can withdraw at any time.

Q:Will I be compensated?

Many clinical trials offer compensation for your time and travel expenses. Specific compensation details will be discussed during the screening process. All study-related medical care is provided at no cost.

Q:Can I leave the trial if I change my mind?

Absolutely. Participation is completely voluntary. You have the right to withdraw from the study at any time, for any reason, without penalty.

Still have questions? Our study coordinators are here to help.

Dystrophic Epidermolysis Bullosa Treatment Options in Rancho Santa Margarita, CA

If you're searching for dystrophic epidermolysis bullosa treatment options in Rancho Santa Margarita, CA, this clinical trial (NCT04917887) may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.

Our Rancho Santa Margarita research site is actively enrolling participants for this clinical trial. You'll receive care from experienced dystrophic epidermolysis bullosa specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.

Looking for more options? Browse all dystrophic epidermolysis bullosa clinical trials near you to find additional studies recruiting in your area.

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