Orange, CANCT06636383Now EnrollingIRB Ready

Glycogen Storage Disease Type Ia Clinical Trial in Orange, CA

Access cutting-edge glycogen storage disease type ia treatment through this clinical trial at a research site in Orange. Study-provided care at no cost to qualified participants.

Sponsored by Ultragenyx Pharmaceutical Inc

Quick Self-Assessment

See if you qualify for this Orange location

Preparing your pre-screening questions…

Expert Care in Orange

Access glycogen storage disease type ia specialists at no cost

IRB Approved

This study follows strict safety protocols and ethical guidelines

No-Cost Care

All study-related glycogen storage disease type ia treatment provided free

Apply for This Orange Location

Check if you qualify for this glycogen storage disease type ia clinical trial in Orange, CA

Secure & Confidential

Your information is protected and will only be shared with the research team.

Why Participate?

  • No-Cost Study Care

  • Local to Orange

    Convenient for CA residents

  • Cutting-Edge Treatment

    Access to innovative therapies

  • Expert Medical Care

    Close monitoring by specialists

  • Possible Compensation*

    For time and travel

*Compensation varies by study. Confirm details with coordinator.

Simple Process

  1. 1Submit this form
  2. 2Phone screening
  3. 3Visit Orange site if eligible
  4. 4Begin participation

About This Glycogen Storage Disease Type Ia Study in Orange

The main objective of this observational study is to evaluate the long-term safety and effectiveness of DTX401 for at least 10 years after DTX401 administration.

Sponsor: Ultragenyx Pharmaceutical Inc

Who Can Participate

Inclusion Criteria

Patient who had:
DTX401 (full or partial dose) administered in a parent clinical study (Group 1) or
Prescribed DTX401(full or partial dose) administered in a post-marketing setting (Group 2)
Patient is willing and able to provide informed consent after the nature of the study has been explained, and prior to any research-related assessments or procedures. If a minor or an adult with cognitive limitations, the patient is willing and able (if possible) to provide assent and have a legally authorized representative provide informed consent after the nature of the study has been explained, and prior to any research-related assessments or procedures.

Exclusion Criteria

Presence of any condition that would interfere with study participation, interpretation of results or affect patient's safety in the opinion of the Investigator

Not sure if you qualify? Submit your interest and a study coordinator will help determine your eligibility.

Frequently Asked Questions

Q:Is this study available in Orange?

Yes, this clinical trial (NCT06636383) has an active research site in Orange, CA that is currently enrolling participants.

Q:Is it safe to participate?

Clinical trials follow strict safety guidelines and ethical standards. This study has been reviewed and approved, and participants are closely monitored by medical professionals. You can withdraw at any time.

Q:Will I be compensated?

Many clinical trials offer compensation for your time and travel expenses. Specific compensation details will be discussed during the screening process. All study-related medical care is provided at no cost.

Q:Can I leave the trial if I change my mind?

Absolutely. Participation is completely voluntary. You have the right to withdraw from the study at any time, for any reason, without penalty.

Still have questions? Our study coordinators are here to help.

Glycogen Storage Disease Type Ia Treatment Options in Orange, CA

If you're searching for glycogen storage disease type ia treatment options in Orange, CA, this clinical trial (NCT06636383) may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.

Our Orange research site is actively enrolling participants for this clinical trial. You'll receive care from experienced glycogen storage disease type ia specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.

Looking for more options? Browse all glycogen storage disease type ia clinical trials near you to find additional studies recruiting in your area.

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Secure · Expert Care · Orange, CA