Durham, NCNCT04454216Now EnrollingIRB Ready

Glycogen Storage Disease VI Clinical Trial in Durham, NC

Access cutting-edge glycogen storage disease vi treatment through this clinical trial at a research site in Durham. Study-provided care at no cost to qualified participants.

Sponsored by Duke University

Quick Self-Assessment

See if you qualify for this Durham location

Preparing your pre-screening questions…

Expert Care in Durham

Access glycogen storage disease vi specialists at no cost

IRB Approved

This study follows strict safety protocols and ethical guidelines

No-Cost Care

All study-related glycogen storage disease vi treatment provided free

Apply for This Durham Location

Check if you qualify for this glycogen storage disease vi clinical trial in Durham, NC

Secure & Confidential

Your information is protected and will only be shared with the research team.

Why Participate?

  • No-Cost Study Care

  • Local to Durham

    Convenient for NC residents

  • Cutting-Edge Treatment

    Access to innovative therapies

  • Expert Medical Care

    Close monitoring by specialists

  • Possible Compensation*

    For time and travel

*Compensation varies by study. Confirm details with coordinator.

Simple Process

  1. 1Submit this form
  2. 2Phone screening
  3. 3Visit Durham site if eligible
  4. 4Begin participation

About This Glycogen Storage Disease VI Study in Durham

Collection and review of clinical information related to Glycogen Storage Disease Type VI (GSD VI) OR Glycogen Storage Disease Type IX (GSD IX) generated during clinic visits.

Sponsor: Duke University

Who Can Participate

Inclusion Criteria

Diagnosis of GSD VI or GSD IX via:
Two variants in the PYGL, PHKA1, PHKA2, PHKG1, PHKG2, or PHKB gene (or one variant with evidence of disease). Note: for males, one variant in the PHKA1 or PHKA2 gene is sufficient for inclusion.
Deficient GP activity or PhK activity per enzymology
Histology as confirmed by clinician
Pregnant women with a diagnosis of GSD VI or GSD IX will be included
Able to provide informed consent for self (adults) or affected individual (minor or adults with a legally authorized representative)
Able to provide consent for release of medical records

Exclusion Criteria

Unable to provide informed consent for participation for one's self or by legally authorized representative/legal guardian/parent

Not sure if you qualify? Submit your interest and a study coordinator will help determine your eligibility.

Frequently Asked Questions

Q:Is this study available in Durham?

Yes, this clinical trial (NCT04454216) has an active research site in Durham, NC that is currently enrolling participants.

Q:Is it safe to participate?

Clinical trials follow strict safety guidelines and ethical standards. This study has been reviewed and approved, and participants are closely monitored by medical professionals. You can withdraw at any time.

Q:Will I be compensated?

Many clinical trials offer compensation for your time and travel expenses. Specific compensation details will be discussed during the screening process. All study-related medical care is provided at no cost.

Q:Can I leave the trial if I change my mind?

Absolutely. Participation is completely voluntary. You have the right to withdraw from the study at any time, for any reason, without penalty.

Still have questions? Our study coordinators are here to help.

Glycogen Storage Disease VI Treatment Options in Durham, NC

If you're searching for glycogen storage disease vi treatment options in Durham, NC, this clinical trial (NCT04454216) may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.

Our Durham research site is actively enrolling participants for this clinical trial. You'll receive care from experienced glycogen storage disease vi specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.

Looking for more options? Browse all glycogen storage disease vi clinical trials near you to find additional studies recruiting in your area.

More Rheumatoid Arthritis Trials in Durham, NC

See all rheumatoid arthritis clinical trials recruiting in Durham — not just this study.

Browse Rheumatoid Arthritis Trials in Durham

Ready to Join in Durham?

Take the first step toward participating in this groundbreaking clinical trial

Secure · Expert Care · Durham, NC