San Diego, CANCT06539507Now EnrollingIRB Ready

Netherton Syndrome Clinical Trial in San Diego, CA

Access cutting-edge netherton syndrome treatment through this clinical trial at a research site in San Diego. Study-provided care at no cost to qualified participants.

Sponsored by BioCryst Pharmaceuticals

Quick Self-Assessment

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Expert Care in San Diego

Access netherton syndrome specialists at no cost

IRB Approved

This study follows strict safety protocols and ethical guidelines

No-Cost Care

All study-related netherton syndrome treatment provided free

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Check if you qualify for this netherton syndrome clinical trial in San Diego, CA

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Your information is protected and will only be shared with the research team.

Why Participate?

  • No-Cost Study Care

  • Local to San Diego

    Convenient for CA residents

  • Cutting-Edge Treatment

    Access to innovative therapies

  • Expert Medical Care

    Close monitoring by specialists

  • Possible Compensation*

    For time and travel

*Compensation varies by study. Confirm details with coordinator.

Simple Process

  1. 1Submit this form
  2. 2Phone screening
  3. 3Visit San Diego site if eligible
  4. 4Begin participation

About This Netherton Syndrome Study in San Diego

This is a first-in-human, Phase 1/1b, 4-part study that includes the evaluation of safety, tolerability, pharmacokinetics (PK), and immunogenicity of BCX17725 when administered via single and multiple doses in healthy adult participants (Parts 1 and 2), and multiple doses in adult participants with Netherton syndrome (Part 3). In Part 4, the effectiveness, safety, and tolerability of BCX17725 when administered via multiple IV and/or SC doses through 12 weeks will be evaluated in adult and adolescent participants with Netherton syndrome.

Sponsor: BioCryst Pharmaceuticals

Who Can Participate

Inclusion Criteria

Male or non-pregnant, non-lactating female aged 18 to 55 years, inclusive (Parts 1 and 2), 18 to 65 years, inclusive (Part 3), or 12 to 65 years, inclusive (Part 4)
Confirmed diagnosis of Netherton syndrome (Parts 3 and 4)
IGA score of ≥ 3 (Parts 3 and 4) and IASI score of ≥ 16 (Part 4)
BMI between 18 and 30 kg/m\^2, inclusive (Parts 1 and 2)
Estimated glomerular filtration rate (eGFR) of ≥ 90 mL/min/1.73 m\^2 (Parts 1 and 2) or ≥ 60 mL/min/1.73 m\^2 (Part 3)
Agree to follow the protocol contraception requirements from screening until 90 days after the last dose of study drug
In the opinion of the investigator, expected to adequately comply with all required study procedures and restrictions for the duration of the study

Not sure if you qualify? Submit your interest and a study coordinator will help determine your eligibility.

Frequently Asked Questions

Q:Is this study available in San Diego?

Yes, this clinical trial (NCT06539507) has an active research site in San Diego, CA that is currently enrolling participants.

Q:Is it safe to participate?

Clinical trials follow strict safety guidelines and ethical standards. This study has been reviewed and approved, and participants are closely monitored by medical professionals. You can withdraw at any time.

Q:Will I be compensated?

Many clinical trials offer compensation for your time and travel expenses. Specific compensation details will be discussed during the screening process. All study-related medical care is provided at no cost.

Q:Can I leave the trial if I change my mind?

Absolutely. Participation is completely voluntary. You have the right to withdraw from the study at any time, for any reason, without penalty.

Still have questions? Our study coordinators are here to help.

Netherton Syndrome Treatment Options in San Diego, CA

If you're searching for netherton syndrome treatment options in San Diego, CA, this clinical trial (NCT06539507) may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.

Our San Diego research site is actively enrolling participants for this clinical trial. You'll receive care from experienced netherton syndrome specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.

Looking for more options? Browse all netherton syndrome clinical trials near you to find additional studies recruiting in your area.

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Secure · Expert Care · San Diego, CA