Recruiting Angelman Syndrome Studies in Boston
About Angelman Syndrome Clinical Trials in Boston
Angelman syndrome is a rare genetic disorder primarily affecting the nervous system, characterized by severe developmental delays, speech impairment, seizures, and a happy demeanor. It is caused by loss of function of the UBE3A gene. Treatment focuses on managing symptoms and maximizing developmental potential.
There are currently 2 angelman syndrome clinical trials recruiting participants in Boston, MA. These studies are seeking a combined 312 participants. Research is being sponsored by Boston Children's Hospital, MavriX Bio, LLC. Clinical trial participation is free and participants receive study-related medical care at no cost.
Angelman Syndrome Clinical Trials in Boston — FAQ
Are there angelman syndrome clinical trials in Boston?
Yes, there are 2 angelman syndrome clinical trials currently recruiting in Boston, MA. Browse the studies on this page to find one that fits.
How do I join a clinical trial in Boston?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Boston research site will contact you about next steps.
Are clinical trials in Boston free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Boston studies also compensate for your time and travel.
What angelman syndrome treatments are being tested?
The 2 active trials in Boston are testing new therapies including novel drugs, biologics, and treatment approaches for angelman syndrome.
Data updated October 12, 2026 from ClinicalTrials.gov