3 Rett Syndrome Clinical Trials in Boston, MA (2026)

Q: How do I join a clinical trial in Boston?

Browse available studies, click one that interests you, and complete the free eligibility form. A study coordinator at the Boston research site will contact you.

Recruiting Rett Syndrome Studies in Boston

NCT05432349Recruiting

Rett Syndrome Registry

The Rett Syndrome Registry is a longitudinal observational study of individuals with MECP2 mutations and a diagnosis of Rett syndrome. Designed together with the IRSF Rett Syndrome Center of Excellenc...

Boston, MA3,000 participantsInternational Rett Syndrome Foundation

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NCT06840496Recruiting

To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome

Primary Objective • To investigate the efficacy of treatment with oral Bionetide versus placebo in girls and women with Rett syndrome Key Secondary Objective • To investigate the efficacy of treatme...

Boston, MAPHASE3210 participantsBiomed Industries, Inc.

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NCT02947971Recruiting

Pilot Study for TCE Imaging of the Esophagus Using an OFDI Capsule With a Compact Imaging System

The goal of this research is to test a distal scanning capsule and a compact redesigned version of the OFDI imaging system in healthy and BE participants to assess ease of use, safety and feasibility ...

Boston, MANA120 participantsMassachusetts General Hospital

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About Rett Syndrome Clinical Trials in Boston

Rett syndrome is a rare genetic neurological disorder that primarily affects girls, causing a regression in development after initially normal growth. It is caused by mutations in the MECP2 gene. Treatment is supportive, with gene therapies under investigation.

There are currently 3 rett syndrome clinical trials recruiting participants in Boston, MA. These studies are seeking a combined 3,330 participants. Research is being sponsored by International Rett Syndrome Foundation, Biomed Industries, Inc., Massachusetts General Hospital. Clinical trial participation is free and participants receive study-related medical care at no cost.

Rett Syndrome Clinical Trials in Boston — FAQ

Are there rett syndrome clinical trials in Boston?

Yes, there are 3 rett syndrome clinical trials currently recruiting in Boston, MA. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Boston?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Boston research site will contact you about next steps.

Are clinical trials in Boston free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Boston studies also compensate for your time and travel.

What rett syndrome treatments are being tested?

The 3 active trials in Boston are testing new therapies including novel drugs, biologics, and treatment approaches for rett syndrome.

Data updated October 16, 2026 from ClinicalTrials.gov