4 Fabry Disease Clinical Trials in Cincinnati, OH (2026)

Q: Are there fabry disease clinical trials in Cincinnati?

Yes, there are 4 fabry disease clinical trials currently recruiting in Cincinnati, OH.

Q: How do I join a clinical trial in Cincinnati?

Browse available studies, click one that interests you, and complete the free eligibility form. A study coordinator at the Cincinnati research site will contact you.

Q: Are clinical trials in Cincinnati free?

Yes, clinical trial participation is always free. Study-related treatments, medical tests, and doctor visits are provided at no cost.

Recruiting Fabry Disease Studies in Cincinnati

NCT06328608Recruiting

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents with Fabry Disease....

Cincinnati, OHPHASE222 participantsChiesi Farmaceutici S.p.A.

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NCT06270316Recruiting

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

The main goals of this clinical study are to characterize safety and PK/PD of AMT-191 i.e. if drug doses used in the study are safe and tolerable and to understand how it acts in the body of people wi...

Cincinnati, OHPHASE120 participantsUniQure Biopharma B.V.

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NCT06858397Recruiting

A proof-of Concept Study to Assess Safety and Tolerability of HM15421/GC1134A in Patients With Fabry Disease

This Phase 1/2 first-in-human (FIH) study is designed to evaluate the safety, tolerability, pharmacokinetics (PK), and efficacy of HM15421 in patients with FD....

Cincinnati, OHPHASE118 participantsGC Biopharma Corp

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NCT06904261Recruiting

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

An open-label study to evaluate the safety, pharmacokinetics (PK), pharmacodynamics (PD), and efficacy of migalastat treatment in pediatric subjects 2 to \< 12 years of age with Fabry disease and with...

Cincinnati, OHPHASE38 participantsAmicus Therapeutics

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About Fabry Disease Clinical Trials in Cincinnati

Fabry disease is a rare genetic disorder caused by deficiency of the enzyme alpha-galactosidase A, leading to accumulation of a fatty substance in cells. It can affect the heart, kidneys, and nervous system. Treatment includes enzyme replacement therapy and chaperone therapy.

There are currently 4 fabry disease clinical trials recruiting participants in Cincinnati, OH. These studies are seeking a combined 68 participants. Research is being sponsored by Chiesi Farmaceutici S.p.A., UniQure Biopharma B.V., GC Biopharma Corp and 1 other organizations. Clinical trial participation is free and participants receive study-related medical care at no cost.

Fabry Disease Clinical Trials in Cincinnati — FAQ

Are there fabry disease clinical trials in Cincinnati?

Yes, there are 4 fabry disease clinical trials currently recruiting in Cincinnati, OH. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Cincinnati?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Cincinnati research site will contact you about next steps.

Are clinical trials in Cincinnati free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Cincinnati studies also compensate for your time and travel.

What fabry disease treatments are being tested?

The 4 active trials in Cincinnati are testing new therapies including novel drugs, biologics, and treatment approaches for fabry disease.

Data updated October 15, 2026 from ClinicalTrials.gov