Cincinnati, OH3 Active Studies

Pompe Disease Clinical Trials in Cincinnati, OH

Find 3 actively recruiting pompe disease clinical trials in Cincinnati, OH. Connect with local research sites and explore new treatment options.

3
Active Trials
2
Sponsors
581
Enrolling

Recruiting Pompe Disease Studies in Cincinnati

NCT06121011Recruiting

A Global Prospective Observational Registry of Patients With Pompe Disease

This is a global, multicenter, prospective, observational registry of patients with Pompe disease, including those with late-onset pompe disease (LOPD) and infantile-onset pompe disease (IOPD). Both u...

Cincinnati, OH500 participantsAmicus Therapeutics
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NCT07123155Recruiting

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

The purpose of this study is to evaluate the safety, pharmacodynamics (PD), and exploratory clinical efficacy of S-606001 in adult participants with LOPD as an add-on to ERT....

Cincinnati, OHPHASE245 participantsShionogi
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NCT04808505Recruiting

A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18

This is a Phase 3, open-label, multicenter study to evaluate the safety, efficacy, PK, PD, and immunogenicity of cipaglucosidase alfa/miglustat treatment in ERT-experienced and ERT-naïve pediatric sub...

Cincinnati, OHPHASE336 participantsAmicus Therapeutics
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About Pompe Disease Clinical Trials in Cincinnati

Pompe disease is a rare genetic disorder caused by accumulation of glycogen in cells due to deficiency of the enzyme acid alpha-glucosidase. It can affect the heart, skeletal muscles, and respiratory system. Treatment includes enzyme replacement therapy.

There are currently 3 pompe disease clinical trials recruiting participants in Cincinnati, OH. These studies are seeking a combined 581 participants. Research is being sponsored by Amicus Therapeutics, Shionogi. Clinical trial participation is free and participants receive study-related medical care at no cost.

Pompe Disease Clinical Trials in Cincinnati — FAQ

Are there pompe disease clinical trials in Cincinnati?

Yes, there are 3 pompe disease clinical trials currently recruiting in Cincinnati, OH. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Cincinnati?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Cincinnati research site will contact you about next steps.

Are clinical trials in Cincinnati free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Cincinnati studies also compensate for your time and travel.

What pompe disease treatments are being tested?

The 3 active trials in Cincinnati are testing new therapies including novel drugs, biologics, and treatment approaches for pompe disease.

Data updated July 20, 2026 from ClinicalTrials.gov