Fairfax, VA7 Active Studies

Fanconi Anemia Clinical Trials in Fairfax, VA

Find 7 actively recruiting fanconi anemia clinical trials in Fairfax, VA. Connect with local research sites and explore new treatment options.

7
Active Trials
5
Sponsors
678
Enrolling

Recruiting Fanconi Anemia Studies in Fairfax

NCT06906367Recruiting

A Study of Patients With Fabry Disease (US Specific)

This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on ...

Fairfax, VA450 participantsAmicus Therapeutics
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NCT06663358Recruiting

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

A multi-centre, multi-country, observational, non-interventional, retrospective and prospective (hybrid) study among Fabry disease participants treated with pegunigalsidase alfa (Elfabrio®) in routine...

Fairfax, VA100 participantsChiesi Farmaceutici S.p.A.
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NCT07712562Recruiting

A Phase 1/2 Study to Evaluate the Safety and Efficacy of Dibotatug (DR-01) in Adults With Bone Marrow Failure Syndromes

This is a multicenter, open-label, Phase 1/2 basket study to evaluate the safety and efficacy of Dibotatug (DR-01) in adults with Bone Marrow Failure syndromes....

Fairfax, VAPHASE160 participantsDren Bio
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NCT06328608Recruiting

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents with Fabry Disease....

Fairfax, VAPHASE222 participantsChiesi Farmaceutici S.p.A.
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NCT06270316Recruiting

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

The main goals of this clinical study are to characterize safety and PK/PD of AMT-191 i.e. if drug doses used in the study are safe and tolerable and to understand how it acts in the body of people wi...

Fairfax, VAPHASE120 participantsUniQure Biopharma B.V.
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NCT06858397Recruiting

A proof-of Concept Study to Assess Safety and Tolerability of HM15421/GC1134A in Patients With Fabry Disease

This Phase 1/2 first-in-human (FIH) study is designed to evaluate the safety, tolerability, pharmacokinetics (PK), and efficacy of HM15421 in patients with FD....

Fairfax, VAPHASE118 participantsGC Biopharma Corp
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NCT06904261Recruiting

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

An open-label study to evaluate the safety, pharmacokinetics (PK), pharmacodynamics (PD), and efficacy of migalastat treatment in pediatric subjects 2 to \< 12 years of age with Fabry disease and with...

Fairfax, VAPHASE38 participantsAmicus Therapeutics
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About Fanconi Anemia Clinical Trials in Fairfax

Fanconi anemia is a rare genetic disorder that affects bone marrow, reducing production of all types of blood cells and increasing cancer susceptibility. It is associated with physical abnormalities and organ defects. Treatment includes blood transfusions, growth factors, and stem cell transplant.

There are currently 7 fanconi anemia clinical trials recruiting participants in Fairfax, VA. These studies are seeking a combined 678 participants. Research is being sponsored by Amicus Therapeutics, Chiesi Farmaceutici S.p.A., Dren Bio and 2 other organizations. Clinical trial participation is free and participants receive study-related medical care at no cost.

Fanconi Anemia Clinical Trials in Fairfax — FAQ

Are there fanconi anemia clinical trials in Fairfax?

Yes, there are 7 fanconi anemia clinical trials currently recruiting in Fairfax, VA. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Fairfax?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Fairfax research site will contact you about next steps.

Are clinical trials in Fairfax free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Fairfax studies also compensate for your time and travel.

What fanconi anemia treatments are being tested?

The 7 active trials in Fairfax are testing new therapies including novel drugs, biologics, and treatment approaches for fanconi anemia.

Data updated November 5, 2026 from ClinicalTrials.gov