4 Friedreich Ataxia Clinical Trials in Philadelphia, PA (2026)

Q: How do I join a clinical trial in Philadelphia?

Browse available studies, click one that interests you, and complete the free eligibility form. A study coordinator at the Philadelphia research site will contact you.

Recruiting Friedreich Ataxia Studies in Philadelphia

NCT06016946Recruiting

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

This project is a global, multicenter, prospective, longitudinal, observational natural history study that can be used to understand the disease progression and support the development of safe and eff...

Philadelphia, PA3,000 participantsFriedreich's Ataxia Research Alliance

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NCT06623890Recruiting

A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors

In this study, researchers will learn more about the safety of BIIB141, also known as omaveloxolone or SKYCLARYS®. This is a drug available for doctors to prescribe for people with Friedreich's Ataxia...

Philadelphia, PA300 participantsBiogen

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NCT06447025Recruiting

An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia

An open label study designed to evaluate the safety, PK, PD, and clinical effects of long-term daily administration of CTI-1601 enrolling adolescent and adult patients with FRDA who have participated ...

Philadelphia, PAPHASE285 participantsLarimar Therapeutics, Inc.

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NCT07180355Recruiting

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

This is a phase 1b, first in-human, open-label, dose-finding study investigating the safety and tolerability of SGT-212 in participants with Friedreich's ataxia (FA). It will be delivered via dual int...

Philadelphia, PAPHASE110 participantsSolid Biosciences Inc.

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About Friedreich Ataxia Clinical Trials in Philadelphia

Friedreich ataxia is a rare inherited disease that causes progressive damage to the nervous system and movement problems. It is caused by reduced frataxin protein from a GAA repeat expansion. Treatment includes supportive care, with omaveloxolone recently approved.

There are currently 4 friedreich ataxia clinical trials recruiting participants in Philadelphia, PA. These studies are seeking a combined 3,395 participants. Research is being sponsored by Friedreich's Ataxia Research Alliance, Biogen, Larimar Therapeutics, Inc. and 1 other organizations. Clinical trial participation is free and participants receive study-related medical care at no cost.

Friedreich Ataxia Clinical Trials in Philadelphia — FAQ

Are there friedreich ataxia clinical trials in Philadelphia?

Yes, there are 4 friedreich ataxia clinical trials currently recruiting in Philadelphia, PA. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Philadelphia?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Philadelphia research site will contact you about next steps.

Are clinical trials in Philadelphia free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Philadelphia studies also compensate for your time and travel.

What friedreich ataxia treatments are being tested?

The 4 active trials in Philadelphia are testing new therapies including novel drugs, biologics, and treatment approaches for friedreich ataxia.

Data updated October 17, 2026 from ClinicalTrials.gov