Recruiting Studies
Advanced SearchData: ClinicalTrials.gov · Source of record for eligibility and locations
Top Cities for Friedreich Ataxia Clinical Trials
Friedreich Ataxia clinical trials are recruiting across 25 cities. Here are the cities with the most active studies:
Friedreich Ataxia Trial Phases
8 research organizations are sponsoring friedreich ataxia trials.
About Friedreich Ataxia
Friedreich ataxia is a rare inherited disease that causes progressive damage to the nervous system and movement problems. It is caused by reduced frataxin protein from a GAA repeat expansion. Treatment includes supportive care, with omaveloxolone recently approved.
Clinical trials are advancing new treatments for friedreich ataxia. Currently, 12 studies are recruiting a combined 4,004 participants across the United States. Research is being conducted by 8 organizations including Friedreich's Ataxia Research Alliance, Biogen, University of Florida and 5 others.
2026 Friedreich Ataxia Research Landscape
As of October 2026, the friedreich ataxia clinical trial landscape includes 12 actively recruiting studies across 25 cities in the United States. These studies are collectively seeking 4,004 participants, with an average enrollment target of 334 per study.
The research spans multiple phases of development: 2 studies are in PHASE2, 2 studies are in PHASE1, 1 study is in PHASE3, 1 study is in NA. The presence of Phase 3 trials indicates that some friedreich ataxia treatments are in late-stage testing and may be approaching regulatory review.
Research is being led by 8 different organizations, including Friedreich's Ataxia Research Alliance, Biogen, University of Florida, Larimar Therapeutics, Inc., Weill Medical College of Cornell University, and 3 others.
Geographically, friedreich ataxia trials are most concentrated in Tampa, Florida (5 trials); Los Angeles, California (4 trials); Gainesville, Florida (4 trials); Philadelphia, Pennsylvania (4 trials); Columbus, Ohio (3 trials) and 7 other cities.
Featured Friedreich Ataxia Studies
Highlighted recruiting studies for friedreich ataxia, selected by enrollment size and research scope.
Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
This project is a global, multicenter, prospective, longitudinal, observational natural history study that can be used to understand the disease progression and support the development of safe and effective drugs and biological products for Friedreich ataxia.
A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors
In this study, researchers will learn more about the safety of BIIB141, also known as omaveloxolone or SKYCLARYS®. This is a drug available for doctors to prescribe for people with Friedreich's Ataxia, also known as FA. This is known as an "observational" study, which collects health information about study participants without changing their medical care. Participants for this study will be found...
Biomarkers in Friedreich's Ataxia
The purpose of this project is to characterize measures of cardiac performance and neuromuscular physiology in FA patients using novel techniques, including echocardiography and magnetic resonance imaging (MRI), metabolic exercise testing, and neurophysiological outcomes.
Frequently Asked Questions About Friedreich Ataxia Clinical Trials
Are there friedreich ataxia clinical trials near me?
Yes, there are 12 friedreich ataxia clinical trials currently recruiting across 25+ cities in the United States, including Tampa, Florida; Los Angeles, California; Gainesville, Florida. Browse the studies above to find one at a location convenient for you.
How do I join a friedreich ataxia clinical trial?
To join a friedreich ataxia clinical trial: 1) Browse the available studies on this page, 2) Click on a study that interests you, 3) Check the study locations to find a site near you, 4) Review the eligibility criteria, and 5) Contact the study site or complete the eligibility form. The process is free and you can withdraw at any time.
Are friedreich ataxia clinical trials free?
Yes, participation in friedreich ataxia clinical trials is free. Study-related treatments, medical tests, and doctor visits are provided at no cost to participants. Many studies also offer compensation for your time and travel expenses.
What types of friedreich ataxia treatments are being studied?
Current friedreich ataxia clinical trials are testing a range of approaches across PHASE2 (2 studies), PHASE1 (2 studies), PHASE3 (1 study), NA (1 study). These include new drugs, combination therapies, medical devices, and other interventions sponsored by 8 research organizations.
Is it safe to participate in friedreich ataxia clinical trials?
Clinical trials are carefully regulated by the FDA and institutional review boards (IRBs). All trials must follow strict safety protocols, and participants receive close medical monitoring throughout the study. You can withdraw from a trial at any time without penalty.
Data updated October 16, 2026 from ClinicalTrials.gov
About This Data
Data: ClinicalTrials.gov · Source of record for eligibility and locations
Clinical trial information on this page is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health (NIH) and National Library of Medicine (NLM). Study data is refreshed every hour to ensure accuracy.
Medical Disclaimer: The information provided on this page is for informational purposes only and does not constitute medical advice. Always consult with a qualified healthcare provider before making decisions about clinical trial participation or changes to your treatment plan.
Page reviewed by the HelloStudys Research Team · Last updated October 16, 2026 · Data from ClinicalTrials.gov