Access cutting-edge diamond blackfan anemia treatment through this clinical trial at a research site in New Hyde Park. Study-provided care at no cost to qualified participants.
Quick Self-Assessment
See if you qualify for this New Hyde Park location
Preparing your pre-screening questions…
Access diamond blackfan anemia specialists at no cost
This study follows strict safety protocols and ethical guidelines
All study-related diamond blackfan anemia treatment provided free
Check if you qualify for this diamond blackfan anemia clinical trial in New Hyde Park, NY
No-Cost Study Care
Local to New Hyde Park
Convenient for NY residents
Cutting-Edge Treatment
Access to innovative therapies
Expert Medical Care
Close monitoring by specialists
Possible Compensation*
For time and travel
*Compensation varies by study. Confirm details with coordinator.
Gene therapy is a new possible treatment for the anemia of DBAS. Gene therapy will soon be available for patients with RPS19-mutated DBAS. This involves inserting the corrected RPS19 gene into the cells, leading to correction of the anemia. The application of gene therapy requires sufficient numbers of stem cells on which the correction can be performed. Stem cells must be mobilized (stimulated to move) from the bone marrow to the peripheral blood and then collected (also called 'harvested'). It is not known if patients with DBAS can mobilize enough stem cells into the peripheral blood to allow for the harvesting of sufficient numbers to permit genetic manipulation. It is important to demonstrate the ability to harvest an adequate number of stem cells before gene therapy can be tried in patients with DBAS. The purpose of this study is to determine if mobilization of stem cells from the bone marrow in patients with DBAS is enough to obtain the numbers of peripheral blood stem cells necessary for effective gene therapy. An actual harvest will not be done.
Sponsor: Northwell Health
Yes, this clinical trial (NCT07186179) has an active research site in New Hyde Park, NY that is currently enrolling participants.
Clinical trials follow strict safety guidelines and ethical standards. This study has been reviewed and approved, and participants are closely monitored by medical professionals. You can withdraw at any time.
Many clinical trials offer compensation for your time and travel expenses. Specific compensation details will be discussed during the screening process. All study-related medical care is provided at no cost.
Absolutely. Participation is completely voluntary. You have the right to withdraw from the study at any time, for any reason, without penalty.
If you're searching for diamond blackfan anemia treatment options in New Hyde Park, NY, this clinical trial (NCT07186179) may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.
Our New Hyde Park research site is actively enrolling participants for this clinical trial. You'll receive care from experienced diamond blackfan anemia specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.
Looking for more options? Browse all diamond blackfan anemia clinical trials near you to find additional studies recruiting in your area.
See all heart attack clinical trials recruiting in New Hyde Park — not just this study.
Browse Heart Attack Trials in New Hyde Park →