Access cutting-edge spinal muscular atrophy (sma) treatment through this clinical trial at a research site in San Diego. Study-provided care at no cost to qualified participants.
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Access spinal muscular atrophy (sma) specialists at no cost
This study follows strict safety protocols and ethical guidelines
All study-related spinal muscular atrophy (sma) treatment provided free
Check if you qualify for this spinal muscular atrophy (sma) clinical trial in San Diego, CA
No-Cost Study Care
Local to San Diego
Convenient for CA residents
Cutting-Edge Treatment
Access to innovative therapies
Expert Medical Care
Close monitoring by specialists
Possible Compensation*
For time and travel
*Compensation varies by study. Confirm details with coordinator.
Spinal muscular atrophy (SMA) is a neurogenetic disorder caused by a loss or mutation in the survival motor neuron 1 gene (SMN1) on chromosome 5q13, which leads to reduced SMN protein levels and a selective dysfunction of motor neurons. SMA is an autosomal recessive, early childhood disease with an incidence of 1:10,000 live births. SMA is the leading cause of infant mortality due to genetic diseases. The purpose of this registry is to assess the long term outcomes of patients with SMA in the context of advances in treatment options and also to characterize and assess long-term safety and effectiveness of OAV-101.
Sponsor: Novartis Pharmaceuticals
Yes, this clinical trial (NCT04174157) has an active research site in San Diego, CA that is currently enrolling participants.
Clinical trials follow strict safety guidelines and ethical standards. This study has been reviewed and approved, and participants are closely monitored by medical professionals. You can withdraw at any time.
Many clinical trials offer compensation for your time and travel expenses. Specific compensation details will be discussed during the screening process. All study-related medical care is provided at no cost.
Absolutely. Participation is completely voluntary. You have the right to withdraw from the study at any time, for any reason, without penalty.
If you're searching for spinal muscular atrophy (sma) treatment options in San Diego, CA, this clinical trial (NCT04174157) may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.
Our San Diego research site is actively enrolling participants for this clinical trial. You'll receive care from experienced spinal muscular atrophy (sma) specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.
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