2 Paroxysmal Nocturnal Hemoglobinuria Clinical Trials in Bethesda, MD (2026)

Q: How do I join a clinical trial in Bethesda?

Browse available studies, click one that interests you, and complete the free eligibility form. A study coordinator at the Bethesda research site will contact you.

Recruiting Paroxysmal Nocturnal Hemoglobinuria Studies in Bethesda

NCT05755867Recruiting

Global PNH Patient Registry

The primary aim of the Global Paroxysmal Nocturnal Hemoglobinuria (PNH) Patient Registry is to conduct a prospectively-planned and efficient natural history study that will result in a more comprehens...

Bethesda, MD500 participantsAplastic Anemia and MDS International Foundation

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NCT07566494Recruiting

Escalating Doses of VAS-101 in Subjects With Stable Sickle Cell Disease

Background: Sickle cell disease (SCD) is an inherited blood disorder. The disease affects the ability of red blood cells to carry oxygen. Research has shown that curcumin, a natural compound found in...

Bethesda, MD25 participantsNational Heart, Lung, and Blood Institute (NHLBI)

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About Paroxysmal Nocturnal Hemoglobinuria Clinical Trials in Bethesda

Paroxysmal nocturnal hemoglobinuria (PNH) is a rare, acquired blood disease where the immune system destroys red blood cells, causing dark-colored urine, fatigue, and blood clots. It is caused by a genetic mutation in blood stem cells. Treatment includes complement inhibitors like eculizumab.

There are currently 2 paroxysmal nocturnal hemoglobinuria clinical trials recruiting participants in Bethesda, MD. These studies are seeking a combined 525 participants. Research is being sponsored by Aplastic Anemia and MDS International Foundation, National Heart, Lung, and Blood Institute (NHLBI). Clinical trial participation is free and participants receive study-related medical care at no cost.

Paroxysmal Nocturnal Hemoglobinuria Clinical Trials in Bethesda — FAQ

Are there paroxysmal nocturnal hemoglobinuria clinical trials in Bethesda?

Yes, there are 2 paroxysmal nocturnal hemoglobinuria clinical trials currently recruiting in Bethesda, MD. Browse the studies on this page to find one that fits.

How do I join a clinical trial in Bethesda?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Bethesda research site will contact you about next steps.

Are clinical trials in Bethesda free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Bethesda studies also compensate for your time and travel.

What paroxysmal nocturnal hemoglobinuria treatments are being tested?

The 2 active trials in Bethesda are testing new therapies including novel drugs, biologics, and treatment approaches for paroxysmal nocturnal hemoglobinuria.

Data updated July 13, 2026 from ClinicalTrials.gov