New York, NEW%20YORK12 Active Studies

Fanconi Anemia Clinical Trials in New York, NEW%20YORK

Find 12 actively recruiting fanconi anemia clinical trials in New York, NEW%20YORK. Connect with local research sites and explore new treatment options.

12
Active Trials
12
Sponsors
61,615
Enrolling

Recruiting Fanconi Anemia Studies in New York

RecruitingNew York, NEW%20YORKNCT00785525

Filgrastim-Mobilized Stem Cells for Transplantation Using Unrelated Donors

The purpose of the study is to: * Establish and evaluate a system for collection of filgrastim-mobilized peripheral blood stem cells from National Marrow Donor Program donors (NMDP) donors * Assess t...

60,000 participants
Center for International Blood and Marrow Transplant Research
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RecruitingNew York, NEW%20YORKNCT06876649

A Master Protocol to Evaluate the Long-Term Safety of (LY3527727) Pirtobrutinib

The master protocol study J2N-MC-JZNY provides a framework to enable the evaluation of the long-term safety and efficacy of pirtobrutinib after completion of clinical studies evaluating pirtobrutinib....

787 participants
Eli Lilly and Company
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RecruitingNew York, NEW%20YORKNCT05714085

Efficacy, Safety, and Pharmacokinetics of Vericiguat in Pediatric Participants With Heart Failure Due to Left Ventricular Systolic Dysfunction (MK-1242-036)

This study aims to compare the efficacy of vericiguat versus placebo on change in n-terminal pro-brain natriuretic peptide (NTproBNP) from baseline to Week 16 of the Base Period. The primary hypothesi...

342 participants
Merck Sharp & Dohme LLC
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RecruitingNew York, NEW%20YORKNCT06783621

A Study to Evaluate Patient Satisfaction With the Overall Face and Neck Appearance After Combined Treatment of OnabotulinumtoxinA, JUVÉDERM® Products, KYBELLA, CoolSculpting Elite and SkinMedica Products

A study to evaluate overall participant satisfaction of face and neck appearance after treatment with onabotulinumtoxinA, JUVÉDERM® products, KYBELLA, CoolSculpting Elite, and select SkinMedica produc...

100 participants
AbbVie
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RecruitingNew York, NEW%20YORKNCT02143830

HSCT for Patients With Fanconi Anemia Using Risk-Adjusted Chemotherapy

The purpose of this study is to determine whether the use of lower doses of busulfan and the elimination of cyclosporine will further reduce transplant-related side effects for patients with Fanconi A...

70 participants
Children's Hospital Medical Center, Cincinnati
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RecruitingNew York, NEW%20YORKNCT05551793

Regeneron AA Multicenter (Dupilumab)

This is a prospective, randomized, double blind, placebo-controlled clinical trial. The study will take place at 4 sites. This trial will enroll a total of 68 patients with moderate to severe AA (affe...

68 participants
Emma Guttman
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RecruitingNew York, NEW%20YORKNCT05004987

Aβ Dynamics in LLMD

This study will examine the biological factors that may modulate the relationship between depression and the development of Alzheimer's disease (AD). Since the direction of causation between depressio...

60 participants
NYU Langone Health
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RecruitingNew York, NEW%20YORKNCT05900050

Efficacy, Safety and Tolerability of VS-01 in Adult Patients With Acute-on-Chronic Liver Failure and Ascites (UNVEIL-IT)®

A Phase 2, multi-center, randomized, controlled, open-label study to evaluate the effects of the intraperitoneal, liposomal formulation VS-01 in patients with an acute episode of hepatic and/or extrah...

60 participants
Versantis AG
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RecruitingNew York, NEW%20YORKNCT06793371

AMBER-HFpEF: Assessment of CK-4021586 in a Multi-Center, Blinded Evaluation of Safety and Tolerability Results in HFpEF

This is a Phase 2 dose-finding study in adult participants with symptomatic HFpEF....

60 participants
Cytokinetics
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RecruitingNew York, NEW%20YORKNCT05919680

A Study of NST-6179 in Subjects With Intestinal Failure-Associated Liver Disease (IFALD).

This is a phase 2a, multicenter, randomized, double-blind, placebo-controlled study to evaluate the safety, tolerability, pharmacokinetics (PK), and pharmacodynamics (PD) of NST-6179 in subjects with ...

36 participants
NorthSea Therapeutics B.V.
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RecruitingNew York, NEW%20YORKNCT05642455

SPEARHEAD-3 Pediatric Study

This is a pediatric basket study to investigate the safety and efficacy of afamitresgene autoleucel in HLA-A\*02 eligible and MAGE-A4 positive subjects aged 2-17 years of age with advanced cancers....

20 participants
Adaptimmune
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RecruitingNew York, NEW%20YORKNCT06270316

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

The main goals of this clinical study are to characterize safety and PK/PD of AMT-191 i.e. if drug doses used in the study are safe and tolerable and to understand how it acts in the body of people wi...

12 participants
UniQure Biopharma B.V.
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About Fanconi Anemia Clinical Trials in New York

Fanconi anemia is a rare genetic disorder that affects bone marrow, reducing production of all types of blood cells and increasing cancer susceptibility. It is associated with physical abnormalities and organ defects. Treatment includes blood transfusions, growth factors, and stem cell transplant.

There are currently 12 fanconi anemia clinical trials recruiting participants in New York, NEW%20YORK. These studies are seeking a combined 61,615 participants. Research is being sponsored by Center for International Blood and Marrow Transplant Research, Eli Lilly and Company, Merck Sharp & Dohme LLC and 9 other organizations. Clinical trial participation is free and participants receive study-related medical care at no cost.

Fanconi Anemia Clinical Trials in New York — FAQ

Are there fanconi anemia clinical trials in New York?

Yes, there are 12 fanconi anemia clinical trials currently recruiting in New York, NEW%20YORK. Browse the studies on this page to find one that fits.

How do I join a clinical trial in New York?

Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the New York research site will contact you about next steps.

Are clinical trials in New York free?

Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many New York studies also compensate for your time and travel.

What fanconi anemia treatments are being tested?

The 12 active trials in New York are testing new therapies including novel drugs, biologics, and treatment approaches for fanconi anemia.

Data updated March 2, 2026 from ClinicalTrials.gov