Access cutting-edge duchenne muscular dystrophy treatment through this clinical trial at a research site in Philadelphia. Study-provided care at no cost to qualified participants.
Access duchenne muscular dystrophy specialists in Philadelphia at no cost
This study follows strict safety protocols and ethical guidelines
All study-related duchenne muscular dystrophy treatment provided free
This is a Phase 2, open-label, multi-center, 2-part study of NS-089/NCNP-02 administered by weekly IV infusion to ambulant boys aged ≥4 to \<15 years with DMD due to mutations amenable to exon 44 skipping. Participants will receive a selected dose of NS-089/NCNP-02 administered once weekly. The study consists of 2 parts: Part 1 and Part 2. Six participants (Cohort 1) will participate in both Part 1 and Part 2, and 14 participants (Cohort 2) will be added for Part 2.
Sponsor: NS Pharma, Inc.
Check if you qualify for this duchenne muscular dystrophy clinical trial in Philadelphia, PA
If you're searching for duchenne muscular dystrophy treatment options in Philadelphia, PA, this clinical trial may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.
Our Philadelphia research site is actively enrolling participants for this clinical trial. You'll receive care from experienced duchenne muscular dystrophy specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.