Bethesda, MDNCT05755867Now EnrollingIRB Ready

Paroxysmal Nocturnal Hemoglobinuria Clinical Trial in Bethesda, MD

Access cutting-edge paroxysmal nocturnal hemoglobinuria treatment through this clinical trial at a research site in Bethesda. Study-provided care at no cost to qualified participants.

Sponsored by Aplastic Anemia and MDS International Foundation

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Expert Care in Bethesda

Access paroxysmal nocturnal hemoglobinuria specialists at no cost

IRB Approved

This study follows strict safety protocols and ethical guidelines

No-Cost Care

All study-related paroxysmal nocturnal hemoglobinuria treatment provided free

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Check if you qualify for this paroxysmal nocturnal hemoglobinuria clinical trial in Bethesda, MD

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Your information is protected and will only be shared with the research team.

Why Participate?

  • No-Cost Study Care

  • Local to Bethesda

    Convenient for MD residents

  • Cutting-Edge Treatment

    Access to innovative therapies

  • Expert Medical Care

    Close monitoring by specialists

  • Possible Compensation*

    For time and travel

*Compensation varies by study. Confirm details with coordinator.

Simple Process

  1. 1Submit this form
  2. 2Phone screening
  3. 3Visit Bethesda site if eligible
  4. 4Begin participation

About This Paroxysmal Nocturnal Hemoglobinuria Study in Bethesda

The primary aim of the Global Paroxysmal Nocturnal Hemoglobinuria (PNH) Patient Registry is to conduct a prospectively-planned and efficient natural history study that will result in a more comprehensive understanding of the disease and its course and pace over time. Other registry objectives include the following: * Provide a convenient online platform for participants (or caregivers) to self-report cases of PNH. * Develop a communications registry within the Global PNH Patient registry (e.g., to notify patients of research studies and clinical trials). * Characterize and describe the Global PNH population as a whole, enhancing the understanding of disease prevalence and phenotype as well as the rate of progression of disease characteristics. * Assist the PNH community with the development of recommendations and standards of care. * Be a case-finding resource to be used for researchers who seek to study the pathophysiology of PNH, retrospectively collate intervention outcomes, and design prospective trials of novel treatments.

Sponsor: Aplastic Anemia and MDS International Foundation

Who Can Participate

Inclusion Criteria

\- Individuals of any age with a confirmed diagnosis of PNH or diagnosis consistent with PNH are eligible for inclusion. PNH is defined as a genetic mutation in the PIG-A gene. Individuals must be willing to provide informed consent. Participants can be:
legal adult participants who are able to provide their own consent;
children and adults unable to provide their own consent, for whom consent must be provided by a Legally Authorized Representative (LAR) who is a legal adult.
Individuals must have at least periodic access to the internet and be able to comply with web-based study procedures and data collections

Exclusion Criteria

Individuals not able to read and understand English.

Not sure if you qualify? Submit your interest and a study coordinator will help determine your eligibility.

Frequently Asked Questions

Q:Is this study available in Bethesda?

Yes, this clinical trial (NCT05755867) has an active research site in Bethesda, MD that is currently enrolling participants.

Q:Is it safe to participate?

Clinical trials follow strict safety guidelines and ethical standards. This study has been reviewed and approved, and participants are closely monitored by medical professionals. You can withdraw at any time.

Q:Will I be compensated?

Many clinical trials offer compensation for your time and travel expenses. Specific compensation details will be discussed during the screening process. All study-related medical care is provided at no cost.

Q:Can I leave the trial if I change my mind?

Absolutely. Participation is completely voluntary. You have the right to withdraw from the study at any time, for any reason, without penalty.

Still have questions? Our study coordinators are here to help.

Paroxysmal Nocturnal Hemoglobinuria Treatment Options in Bethesda, MD

If you're searching for paroxysmal nocturnal hemoglobinuria treatment options in Bethesda, MD, this clinical trial (NCT05755867) may be an excellent opportunity. Clinical trials provide access to cutting-edge treatments that aren't yet available to the general public, often at no cost to participants.

Our Bethesda research site is actively enrolling participants for this clinical trial. You'll receive care from experienced paroxysmal nocturnal hemoglobinuria specialists who are at the forefront of medical research. All study-related care, including examinations, treatments, and monitoring, is provided at no cost to qualified participants.

Looking for more options? Browse all paroxysmal nocturnal hemoglobinuria clinical trials near you to find additional studies recruiting in your area.

More Paroxysmal Nocturnal Hemoglobinuria Trials in Bethesda, MD

See all paroxysmal nocturnal hemoglobinuria clinical trials recruiting in Bethesda — not just this study.

Browse Paroxysmal Nocturnal Hemoglobinuria Trials in Bethesda

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